The new edition of “Rare Diseases & Orphan Drugs” is already published. The current issue focuses on the global activities in the rare diseases field. Prof. Hanns Lochmueller, Dr. Stephen Groft and Assoc. Prof. Yukiko Nishimura will share their opinion on these topics. You will also learn about the gene therapy, the rare disease spina bifida and what is going with the epidemiological registries for rare diseases in Bulgaria. Have a nice time with “Rare Diseases & Orphan Drugs”!
Rare Diseases and Scientific Inquiry